Tran H, Moazami MP, Yang H, McKenna-Yasek D, Douthwright C, Pinto C, Metterville J, Shin M, Sanil N, Dooley C, Puri A, Weiss A, Wightman N, Gray-Edwards H, Marosfoi M, King RM, Kenderdine T, Fabris D, Bowser R, Watts JK, Brown RH. Potent Mixed Backbone Antisense Oligonucleotide Safely Suppresses Expression of Mutant C9ORF72 Transcripts and Polydipeptides: First in Human Pilot Study. Research Square preprint, February 21 2021. Research Square.

Recommends

Please login to recommend the paper.

Comments

No Available Comments

Make a Comment

To make a comment you must login or register.

This paper appears in the following:

News

  1. FTD Fluid Markers for Degeneration: Check. For Pathology: Not Yet.